The Duchenne community is working closely together to prepare for the April 25 Advisory Committee Meeting for Sarepta’s therapy eteplirsen. PPMD, the Duchenne Alliance, the Center for DMD at UCLA, Jett Foundation, and the Race to Yes have put together a short video so that you can learn about the different ways you can become involved in this historic event. Whether submitting written testimony, attending the Ad Comm in person, participating in the Open Public Hearing, or doing all three, this community is strongest when we work together and collaborate. After watching this video, if you have any questions, do not hesitate to reach out to
or visit http://www.MakeDuchenneHistory.com for more information on how you can get involved. Together, we will end Duchenne.
Tags duchenne duchenne muscular dystrophy dmd becker bmd muscular dystrophy dbmd sarepta eteplirsen fda ad comm advisory committee ppmd race to yes cdmd jett foundation parent project muscular dystrophy
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together concert conspire cooperate coproduce do business with get together glue oneself to go partners hook on hook up interface join forces join together join up with participate team up throw in together throw in with tie in work with abet advance agree back up band befriend coadjute coincide collaborate combine comply with conduce contribute coordinate espouse forward further go along with help league lend a hand partner pitch in play ball pool resources pull together second share in show willingness side with stick together succor take part unite uphold work side by side work together administer allot apportion assign bestow come across with deliver disburse dish out dispense disperse disseminate divide divvy dole out drop fork out fork over give hand out impart inflict measure mete out partition render reward strike absorb allure arrest bewitch busy captivate catch charm draw embark on employ enamor enchant enter into enthrall fascinate give a try give a whirl go for broke go in for go out for grip have a fling at have a go at have a shot at imbue immerse interest involve join keep busy monopolize practice preengage preoccupy set about soak tackle tie up try on for size undertake be a party to be in on consume devour feed get in the act have a finger in ingest receive sample savor sip sit in on take attack begin buckle down come through commence contribute work do one's bit fall to get cracking get going go to it help; get busy hop to it jump in launch plunge into set to subscribe tee off volunteer wade in deal comic sudden tense affecting breathtaking climactic dramaturgic dramaturgical effective electrifying emotional expressive farcical histrionic impressive melodramatic powerful sensational spectacular startling striking suspenseful the histrionical The Sarepta comms comm Duchenne sinewy burly sturdy brawny stout robust wiry hefty husky lusty mighty strong tiger tough hulky ripped ropy small thin weak beastly bestial bodily brute brutish corporeal earthly earthy feral fleshy mammalian muscular natural physical sensual untamed wild zoological able-bodied active energetic fit powerful strapping vigorous athletic beefcake beefy big bruising bulky gorillalike hulking hunk portly stocky thickset well-built coarse fibroid hairy pulpy stalky threadlike tissued veined woody able acclimatized capable enduring firm fresh hale hardened healthy hearty in fine fettle in good condition in good shape indefatigable inured physically fit resistant rugged seasoned solid sound stalwart staunch substantial tenacious unflagging well all right blooming bright-eyed bushy-tailed chipper flourishing full of life hardy healthful in fine feather in the pink lively normal potent restored rosy-cheeked safe and sound trim unimpaired virile whole animal fibrous DMD dmd Becker Beckers becker BMD B.M.D bmd BMDS Sarepta FDA FDAS F.D.A. comms comm helping advising a few words of wisdom admonition advisory caution light caveat deterrent example enough said forewarning hint lesson message moral omen portent red flag sign of things to come wake-up call warning word to the wise academic donnish edifying enlightening exhortative expository homiletic hortative instructive moralizing pedagogic pedantic preachy preceptive schoolmasterist sermonic sermonizing teacherish teacherly teachy chatty communicative descriptive educative elucidative explanatory forthcoming gossipy illuminating informational instructional newsy revealing revelatory significant advertisement alert bulletin communication communique declaration information news notice proclamation release report statement custodial guardian protective tutelar admonishing admonitory cautioning preventive cautionary tale didactic informative notification tutelary cautionary Advisory chamber cabinet bureau board jury panel council President admiral advisers chair chairperson chargé d'affaires command commander committee consulate department directors embassy executive executives feds front office general governing body headquarters legislature management ministry officers officials powers presidency presidium stewards superintendents supervisors top brass upstairs advisory group brass conclave directorate execs executive suite trustees agency authority commission division office salt mines service setup shop store administration administrators assembly assistants brain trust bureaucracy counselors department heads government kitchen cabinet official family commissioners delegation deputation representative ppmd run relay match event chase rush clash clip dash spurt meet issue tribe family people color house strain seed folk breed type stock nation blood line clan kind kin parent rill duct tide gill fly shoot hurry gallop tear dart bolt sprint hustle career boil swoop whisk course pursue fling haste scud skim hie lash post hasten wing bustle walk slow dally dawdle delay wait stay ancestor antecedent antecessor breeding derivation descent extraction forebear forefather foregoer foremother forerunner genealogy heritage kindred lineage origin parentage pedigree precursor primogenitor progenitor race source ancestry background forebears heritance legacy position rank station status brand character feather genus ilk likes lot nature number progeny sort species stamp stripe variety orbit passage pilgrimage procedure progress cultural level degree estate grade order social order sphere standing stratum hunt hunting quest venery birth caste Race black people white people asian people humans horacio badass awesome rad amazing best friend rasists white black asian african-american native american good okay amen yea fine aye gladly surely true yep disagreed accepting acknowledgment acquiring admission approval assent compliance consent cooperation gaining getting go-ahead green light nod obtaining permission receipt receiving reception recognition securing taking on undertaking yes accede accept accommodate adapt adjust agree allow approve bow to buy cave in come across come around comply concur conform cry uncle cut a deal ditto give in give out go along jibe pass play ball reconcile roll over and play dead say uncle set shake on submit subscribe yield acknowledge acquiesce admit be of the same mind bury the hatchet buy into check clinch the deal come to terms concede engage give blessing give carte blanche give green light give the go-ahead go along with grant make a deal pass on permit recognize see eye to eye settle side with sign take one up on accord acquiescence allowance authorization blank check blessing carte blanche concurrence leave right on sanction say so stamp of approval sufferance understanding bless fold give the nod give up knuckle under let roll over say yes sign off on throw in the towel acknowledged admitted assumed indeed just so acceptance granted Yes date girl rejected rejection fredfredburger reason word Jett jett base heart bottom root guts bed prop reason basics foot stay nub ground ABCs fear top company society charity guild set-up alliance association circle council federation foundation fraternity institute league basis spine support vertebrae vertebral column authority backbone chief constituent core essence essential evidence fundamental groundwork important part infrastructure key origin primary element principal principle source underpinning account agency aim antecedent author beginning causation consideration creator determinant doer element end explanation genesis grounds incitement inducement instigation leaven mainspring maker matter motivation motive object occasion prime mover producer purpose spring stimulation architecture arrangement assembly build cast composition conception constitution contour cut development disposition edifice elevation erecting erection fabric fabricating fabrication figuration figure form format formation improvisation invention makeup making manufacture mold origination outline plan planning prefab prefabrication putting up raising rearing roadwork shape structure system systematization turn type amount body bottom line bulk burden consequence corpus crux focus import importance kernel main idea mass meat meat and potatoes middle midpoint midst nitty gritty nucleus pith pivot purport quick significance staple substance thrust upshot academy cause construction father mother origin center author root source folks cause child end au pair babysitter caretaker custodian governess nanny nurse parent actualize beget bring into being bring into existence bring to pass build cause to be coin compose conceive concoct constitute construct contrive design devise discover dream up effect erect establish fabricate fashion forge form formulate found generate give birth to give life to hatch imagine initiate institute invent invest make occasion organize originate perform plan procreate produce rear set up shape sire spawn start daddy old man papa pappy pop ancestor begetter dad forebearer padre predecessor procreator progenitor antecedent ascendant forerunner founder materfamilias matriarch originator paterfamilias patriarch precursor primogenitor relative accomplish achieve bear breed bring about develop engender get up give rise to inaugurate induce introduce multiply muster propagate provoke reproduce whip up work up caregiver create parents Parents task deal job plan pet setup aim thing baby feat fun see devise image design draft scheme frame intend reckon chart cast gauge think vision ignore forget keep extend poke pout jut beetle shoot fling hurl pitch heave take act avocation bag ballgame bit deed endeavor enterprise entertainment game hobby labor occupation pastime project racket scene stunt trip undertaking venture work zoo assignment calling case circumstance concern duty employment episode event hap happening incident interest mission obligation occurrence office function proceeding profession province pursuit question realm responsibility subject topic transaction adapt adjust agree to blueprint come to terms compromise concert construct contrive decide determine direct establish get act together get ready hammer out a deal harmonize iron out lay out line up make a connection make ready manage map out negotiate organize prepare promote provide pull a wire pull things together quarterback resolve schedule set stage settle shape up tailor work out work out a deal breed compound concoct develop excite foment form gather hatch impend loom mull plot start stir up weave abut border bound communicate join meet neighbor protrude verge boot bung chuck drive drop fire impel launch lob peg shed shy sling thrust toss activity affair arrange brew butt Projects projects gangstas drugs pimps hookers ghetto dirty buildings hood trap the struggle hoes gangbangers drug dealers slum pj&39;s ject jects